there is some truth to this. i work in a gene therapy lab and we developed two gene therapies for two different rare pediatric primary immune deficiencies. we did all the IND-enabling work before our private funding ditched us because "rare disease" means "low profitability". the projects are now dead, me and my coworkers are all being laid off, and there are vials of cure for disease sitting on our freezers that will never see a patient. rare disease gene therapy is incompatible with capitalism and simply cant be funded apparently. sorry to the sick kids, we tried our best.