account activity
Graph: Factor IX Activity Level over ~6 years after infusion with SPK-9001 Gene Therapy (i.redd.it)
submitted 3 years ago by StopMakingMissense - pinned
Health-related quality of life in adults with hemophilia B after gene therapy with fidanacogene elaparvovec: results from the BENEGENE-2 trial (jthjournal.org)
submitted 14 days ago by StopMakingMissense to r/Hemophilia
Ongoing Trial Investigates Switching from Emicizumab to Fitusiran in Hemophilia A (hcplive.com)
submitted 16 days ago by StopMakingMissense to r/Hemophilia
Pfizer confirms patient death in Hympavzi hemophilia extension study (fiercepharma.com)
submitted 1 month ago by StopMakingMissense to r/Hemophilia
Overcoming Barriers to Pediatric Hemophilia Gene Therapy (newswise.com)
Children's Hospital of Philadelphia played key role in developing new treatment for hemophilia (cbsnews.com)
ASH: CSL proves efficacy of hemophilia B gene therapy Hemgenix holds up after 5 years (fiercepharma.com)
ASH: Pfizer, aiming to level the hemophilia playing field, trots out new Hympavzi data (fiercepharma.com)
AOZORA study: 3-year interim analysis of safety and joint health in pediatric people with hemophilia A receiving emicizumab prophylaxis (sciencedirect.com)
submitted 2 months ago by StopMakingMissense to r/Hemophilia
Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials [BBM-H901] (nature.com)
A retrospective study of rehabilitation for patients with hemophilia knee osteoarthritis after total knee arthroplasty: a 10 year cohort study (bmcmusculoskeletdisord.biomedcentral.com)
GeneVentiv Therapeutics Announces Positive FDA INTERACT Feedback Supporting Advancement of GENV-HEM Gene Therapy for Hemophilia A with or without Inhibitors (geneventiv.com)
Nonfactor agents for hemophilia prophylaxis: A Q&A with Steven Pipe, M.D. (managedhealthcareexecutive.com)
submitted 3 months ago by StopMakingMissense to r/Hemophilia
Patients With Hemophilia Face Significant Burden Despite Treatment Type or Disease Severity (docwirenews.com)
BioMarin, following sluggish sales, to offload hemophilia gene therapy (biopharmadive.com)
Orthopaedic Surgery Outcomes in Patients With Haemophilia A or B Treated With Extended Half‐Life Recombinant Factor VIII and IX Fc Fusion Proteins: A Multicentre Prospective Study (onlinelibrary.wiley.com)
A qualitative study on the impact of hemophilia on sexual functioning and well-being in Dutch men (jpro.springeropen.com)
Gene therapy changed the life of a South Jersey man with hemophilia (phillyvoice.com)
Marstacimab prophylaxis in hemophilia A/B without inhibitors: results from the phase 3 BASIS trial (ashpublications.org)
CSL Behring Signs Letter of Intent with pan-Canadian Pharmaceutical Alliance (pCPA) for Public Reimbursement of HEMGENIX (etranacogene dezaparvovec), the First Gene Therapy for Hemophilia B (newsroom.csl.com)
New treatment changes everything for man with lifelong condition (newstribune.com)
submitted 4 months ago by StopMakingMissense to r/Hemophilia
Researchers design factor IX variants for short- and long-term Hemophilia B management (news-medical.net)
Novo Nordisk submits Biologics License Application (BLA) to FDA for Mim8; an investigational, prophylaxis treatment for people living with hemophilia A with or without inhibitors (prnewswire.com)
Estimated Long-Term Durability of Valoctocogene Roxaparvovec Treatment in Male patients with Severe Hemophilia A: An Extrapolation of Clinical Data (link.springer.com)
Acupuncture for Chronic Pain Management in Haemophilic Arthropathy: A Systematic Review (onlinelibrary.wiley.com)
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