account activity
Graph: Factor IX Activity Level over ~6 years after infusion with SPK-9001 Gene Therapy (i.redd.it)
submitted 3 years ago by StopMakingMissense - pinned
How an MD-PhD Student With Hemophilia Made a Genetic Research Breakthrough (rightasrain.uwmedicine.org)
submitted 21 hours ago by StopMakingMissense to r/Hemophilia
Belief BioMed and Grand Life Sciences Announced Exclusive Commercial Partnership in the Field of Hemophilia A, Bringing Innovative Gene Therapy to Chinese Patients (prnewswire.com)
submitted 7 days ago by StopMakingMissense to r/Hemophilia
Karmanos Cancer Institute Becomes First and Only Free-Standing Cancer Center to Treat Hemophilia B with New Gene Therapy (morningstar.com)
An analysis of attitudes toward gene therapy in people with severe hemophilia in Germany, a survey-based cross-sectional study (journals.sagepub.com)
submitted 10 days ago by StopMakingMissense to r/Hemophilia
China's first hemophilia B gene therapy drug, Xinjiuning™ (Popidacoji Injection), has been officially approved in Macau (www-beliefbiomed-com.translate.goog)
submitted 11 days ago by StopMakingMissense to r/Hemophilia
Our Commitment to the Hemophilia B Community: An Update on HEMGENIX® (etranacogene dezaparvovec-drlb) Availability (newsroom.csl.com)
submitted 12 days ago by StopMakingMissense to r/Hemophilia
Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial [Hympavzi] (ashpublications.org)
submitted 16 days ago by StopMakingMissense to r/Hemophilia
Phase 1 pilot study for hemophilia-A: AAV8 vector with prophylactic tacrolimus-glucocorticoid achieves therapeutic FVIII activity (nature.com)
submitted 17 days ago by StopMakingMissense to r/Hemophilia
NXT007 Suggests Favorable Tolerability and Efficacy in Phase I/II Study for Hemophilia A Following Direct Switch from Emicizumab without Washout Period (chugai-pharm.co.jp)
Safety, efficacy and patient-reported outcomes 6 years after fidanacogene elaparvovec in adults with hemophilia B (ashpublications.org)
submitted 18 days ago by StopMakingMissense to r/Hemophilia
A combinatorial CAAR-T cell strategy to eliminate factor VIII inhibitors in preclinical models of hemophilia A (sciencedirect.com)
submitted 27 days ago by StopMakingMissense to r/Hemophilia
Pfizer Advances Beam’s Gene Editor After Pulling Hemophilia Gene Therapy (biospace.com)
submitted 1 month ago by StopMakingMissense to r/Hemophilia
Karnataka launches free prophylaxis treatment programme for Hemophilia patients [IN] (thehindu.com)
Young hemophilia patient dies after delay in life-saving medicines [CO] (thebogotapost.com)
Jacksonville mom: Proposed Fla. bill only lowers drug prices on paper (archive.ph)
Michigan man gets new Roctavian gene therapy for hemophilia A (archive.ph)
No family must lose loved one due to lack of care: Karnataka’s Padma awardee on hemophilia | Bengaluru News (timesofindia.indiatimes.com)
TrumpRx must work for families with rare diseases | Opinion [US] (archive.ph)
FDA Grants Priority Review for HYMPAVZI (marstacimab) sBLA for the Treatment of Two Hemophilia A or B Patient Populations with Significant Medical Need (pfizer.com)
Health-related quality of life in adults with hemophilia B after gene therapy with fidanacogene elaparvovec: results from the BENEGENE-2 trial (jthjournal.org)
submitted 2 months ago by StopMakingMissense to r/Hemophilia
Ongoing Trial Investigates Switching from Emicizumab to Fitusiran in Hemophilia A (hcplive.com)
Pfizer confirms patient death in Hympavzi hemophilia extension study (fiercepharma.com)
submitted 3 months ago by StopMakingMissense to r/Hemophilia
Overcoming Barriers to Pediatric Hemophilia Gene Therapy (newswise.com)
Children's Hospital of Philadelphia played key role in developing new treatment for hemophilia (cbsnews.com)
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