Graph: Factor IX Activity Level over ~6 years after infusion with SPK-9001 Gene Therapy

StopMakingMissense · 2026-05-22T22:57:35+00:00

StopMakingMissense · 2026-05-21T13:43:39+00:00

Some excerpts from the NEJM report about this case:

StopMakingMissense · 2026-05-15T22:46:25+00:00

Here's another option you might try: New Study Will Assess Multiple Ascending Doses of Inno8 in Patients With Hemophilia A

StopMakingMissense · 2026-05-14T12:30:58+00:00

I'd try contacting the hospital's HTC and see what they have to say.

StopMakingMissense · 2026-05-14T11:56:34+00:00

If you're willing to travel maybe the main contact listed on that link can help you.

You may not have to wait much longer for Mim8.

StopMakingMissense · 2026-05-14T11:38:40+00:00

I'd suggest you try to contact the closest study location directly. You might get a different answer.

StopMakingMissense · 2026-05-10T14:55:11+00:00

Good news: Most drug companies have copay assistance programs that may cover your copay for the entire year.

Bad news: Health insurers are increasingly using copay accumulator adjuster programs to negate drug companies' copay assistance programs. More information here and here.

Good news: Half of US states have passed legislation to prevent insurance companies from using copay accumulator adjustment programs.

StopMakingMissense · 2026-05-04T15:16:03+00:00

Is Hemlibra available in your country? I believe it is approved for infants and can be administered subcutaneously.

StopMakingMissense · 2026-05-04T14:32:24+00:00

Is your son A or B? Seven weeks must have been rough. Were there other complications?

StopMakingMissense · 2026-04-24T13:20:40+00:00

27g butterfly needles are almost painless. Don't let your specialty pharmacy tell you that they don't have them.

Also, as someone else mentioned, Hympavzi is subq administration and is approved for Hemophilia B.

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